Conferences \ BioProcessing, Biologics & Biotherapeutics Congress \ Cell & Gene Therapeutics \ Agenda \ Harald Petry |
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Alipogene Tiparvovec: The First Gene Therapy for a General Metabolic DisorderWednesday, 20 July 2011 at 14:15 Add to Calendar ▼2011-07-20 14:15:002011-07-20 15:15:00Europe/LondonAlipogene Tiparvovec: The First Gene Therapy for a General Metabolic DisorderSELECTBIOenquiries@selectbiosciences.com During the presentation the various steps to develop a gene therapy medicinal product, will be discussed. Alipogene tiparvovec in LPLD will be used to demonstrate that persistent gene transduction after one-time intramuscular administration is feasible, and results in long term clinical improvements in the ‘chylomicronaemia syndrome’ caused by LPLD. |